
Development of a Lentiviral Gene Therapy for Alpha Thalassemia
Donald B. Kohn & Eva Segura, PhD Candidate Tuesday, November 7, 2023, 8:00-9:00 am (San Francisco) Check your time zone […]
Imagine a world where genetic and anatomic birth defects can be identified, treated, or even cured in utero. A world where the repertoire of fetal therapy expands from the current surgical techniques to encompass stem cell, protein replacement, and genetic therapies for devastating genetic diseases.
Breakthroughs in genetic sequencing, gene editing, and maternal-fetal immunology have brought us closer than ever to this vision. As the institution that performed the first human fetal surgery, we are in the best position to push the frontiers of this innovative field.
The Center for Maternal-Fetal Precision Medicine is developing research studies and clinical trials aimed at understanding, and ultimately curing, a host of fetal and congenital diseases.